We are developing REN001 to modulate genes critical to metabolism and generation of ATP, which is the primary source of energy for cellular processes. We are initially developing REN001 in three rare genetic diseases that typically present with myopathy and have high unmet medical need: primary mitochondrial myopathies (PMM), long-chain fatty acid oxidation disorders (LC-FAOD), and glycogen storage disease type V (McArdle disease). Our experienced team of drug development experts, are dedicated and passionate about finding effective therapies for these complex rare genetic mitochondrial diseases.